The agency said it approved leucovorin for children and adults with a genetic condition that limits delivery of folate, an essential form of vitamin B, to the brain. FDA officials estimate the ...

Lebanese leaders and aid groups warned of a growing humanitarian crisis, with nearly 700,000 people displaced as Israel targets Hezbollah. Defense Secretary Pete Hegseth predicted the most intense day ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Researchers from Japan have uncovered direct evidence showing how ketamine exerts its rapid antidepressant effects in ...

Stomach ulcers, also known as peptic ulcers, are open sores in the lining of your stomach or the upper part of your small intestine. The ulcer forms when stomach acid eats away at the mucus that ...

Kidney stones are not just a painful one-time event but often signal deeper health imbalances. Experts warn they frequently recur, with a 50% chance within five years. Dehydration, high-salt diets, ...

Emerging modalities such as self-amplifying and circular RNA, expanding oncology and rare-disease applications, and scalable manufacturing are creating high-growth investment avenues, supported by ...

Food trends appear almost every year, but only a few stand the test of science and time. One eating pattern that continues to draw attention from doct.

Among treatment-naïve adults with obesity-hypoventilation syndrome, a combination of acetazolamide and atomoxetine taken for 2 weeks improved hypoventilation and sleep-related breathing, according to ...

Scientists usually study the molecular machinery that controls gene expression from the perspective of a linear, two-dimensional genome—even though DNA and its bound proteins function in three ...

Beam Therapeutics Inc. buy thesis: base-editing gene therapy leaders, risto-cel & BEAM-302 catalysts, strong cash runway.

February 25, 2026 marks one year since KJ, an infant born with severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, became the world's first person to receive a personalized CRISPR-based gene ...