Apitegromab improved motor function in SMA patients in a Phase 3 trial analysis, with stronger benefits seen in those treated earlier.

The last patient in Lundbeck’s phase 3 clinical trial, MASCOT, has been randomised ahead of schedule in a study evaluating amlenetug as a potential treatment for multiple system atrophy (MSA). The ...

NMD Pharma will also present an update on the ongoing SYNAPSE-MG Phase 2b clinical trial of ignaseclant in generalized myasthenia gravisAarhus, ...

This article was reviewed by Julia Switzer, MD, FACOG. Key Takeaways: Changes to the labia minora in menopause can include thinning, paleness, and dryness. This happens ...

Leigh-Anne Pinnock has spoken about her former Little Mix bandmate Jesy Nelson's twin's heartbreaking SMA diagnosis after it was revealed that all of the girls had reached out to her ...

Leeds United supporters feel the FA has shown double standards after Daniel Farke's one-match ban ...

Leeds United supporters have accused the FA of inconsistency after Rodri avoided a ban for questioning a referee’s neutrality. Five weeks after Manchester City’s 2-2 draw with Tottenham on 1 February, ...

The FDA proposes new rules allowing mutation-specific gene therapies to qualify for approval despite extremely small patient ...

The 34-year-old singer claimed that after learning about her former bandmates twin daughters heartbreaking diagnosis, she reached out to support her ...