Data presented at the 2026 Muscular Dystrophy Association meeting could have readthroughs to companies developing therapies ...
Chronic obstructive pulmonary disease (COPD) is known for causing breathing difficulties and limiting everyday activities.
On World Rare Disease Day, we take a look at Pompe disease - a rare genetic disorder caused by a deficiency of the GAA enzyme, leading to glycogen buildup in muscles. It results in progressive muscle ...
A new experimental drug, Nerandomilast, has shown potential in reducing lung inflammation and fibrosis in preclinical models of Idiopathic Inflammatory Myopathy–Associated Interstitial Lung Disease ...
Interim observations from the Phase 2 TRAILHEAD study show continued improvement in handgrip strength, overall stability of elbow and shoulder strength in new dynamometry measurements Greater ...
At the 2026 MDA Conference in Orlando, Genethon unveiled new two‑year efficacy data for its gene therapy candidate GNT0004, a key milestone for Duchenne muscular dystrophy research.
BridgeBio Pharma has taken another step toward the potential approval of its muscle weakness drug candidate BBP-418, ...
Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal ...
March 4 (Reuters) - PepGen said on Wednesday that the U.S. Food and Drug Administration has placed a partial clinical hold on its mid‑stage trial of a rare muscle disease drug, sending its shares ...
A RECOMMENDATION for the HSE not to cover the cost of a drug to help children with a rare muscular disease has been blasted by families. Last year, The Irish Sun highlighted the plight of ...
Muscle matters more than most people think, and building lean mass works like installing a protective buffer for the years ...
A species of gut bacteria called Roseburia inulinivorans is specifically associated with human muscle strength and improved muscular performance in mice, finds research published online in the journal ...