It consisted of 18 women participating in a 5-day dry immersion test to assess the risk of developing potentially life-threatening blood clots. The results support existing evidence that women are at ...

Biogen’s successor to Spinraza (nusinersen) has shown benefit in spinal muscular atrophy (SMA) patients who had suboptimal clinical status despite prior administration of gene therapy. In the Phase Ib ...

Barclays 28th Annual Global Healthcare Conference March 12, 2026 8:30 AM EDTCompany ParticipantsDavid Hallal - ...

When winter sets in and food becomes scarce, some mammals hibernate, entering a state of deep rest that slashes their energy needs and allows them to fast for months. However, fasting deprives them of ...

Data presented at the 2026 Muscular Dystrophy Association meeting could have readthroughs to companies developing therapies ...

Isro and the All India Institute of Medical Sciences (AIIMS) have signed an MoU to collaborate on space medicine research aimed at supporti.

Jesy Nelson's Little Mix bandmate, Leigh-Anne Pinnock, has opened up about Jesy's twins' diagnosis. Earlier this year, Jesy took to Instagram to announce her twin girls, Ocean Jade and Story Monroe ...

Permanent; Fitzroy location; Challenging and rewarding work environment; About the Role An opportunity is available for a Grade 3 Physiotherapist to join the ...

SMA mutations disrupt spinal cord development, with fewer nerve cells in early stages. SMN protein deficiency leads to a mesodermal fate bias, with fewer motor neurons. Increasing SOX2 pathway ...

More early-stage data show the drug, called salanersen, appeared to have positive effects on neurodegeneration and motor function in patients previously treated with Novartis' Zolgensma.

STELLAR-2, a randomized, double-blind, sham-controlled study, will evaluate the effects of salanersen when initiated ~6 months after onasemnogene abeparvovec-xioi in infants with SMA who received ...

Scholar Rock’s latest earnings call struck a cautiously optimistic tone, with management emphasizing regulatory traction, a deepening neuromuscular pipeline, and a visibly maturing commercial ...