Leigh syndrome is a rare metabolic disorder that begins in childhood and causes severe neurological and muscular problems. The disease has long been considered untreatable. In a pilot study involving ...

Stem cell therapy, or regenerative medicine, uses stem cells or their derivatives to repair, replace, or regenerate diseased, ...

Keros Therapeutics will use the Massachusetts General Hospital MyMatch program to design a clinical trial testing rinvatercept for ALS.

Simple field-based tests of muscle strength can provide early clues about the risk of developing several long-term illnesses.

Stem cells possess unique capabilities in contemporary medicine. Stem cells have the potential to develop various cell types, ...

Solid Biosciences (SLDB) stock retains a "Strong Buy" rating, driven by robust interim data for SGT-003 in pediatric Duchenne ...

Clinical & Scientific Conference, researchers and clinicians are talking about the central role of patients, families, and caregivers in driving change for people living with neuromuscular diseases.

Incubated by Atlas Venture, the biotech startup is advancing a daily pill it sees potentially helping people with dystonia or ...

The following segment was excerpted from the Harbor Health Care ETF Q4 2025 Commentary.During the fourth quarter, the Harbor Health Care ETF ...

Background Gut bacteria have been implicated in a wide range of health conditions, yet their potential role in preventing and treating muscle-wasting disorders remains largely unexplored. Objective We ...

Sildenafil—an active ingredient also marketed under the name of Viagra—improves symptoms in patients with Leigh syndrome.

Sildenafil – an active ingredient also marketed under the name of Viagra – improves symptoms in patients with Leigh syndrome. This has now been reported in the Cell* journal by researchers at Charité ...