This Monday 9 March, the nation is invited to celebrate National Meatball Day with purpose, by turning its love of meatballs ...

UCL’s Professor Francesco Muntoni has received the 2026 Novo Nordisk Prize for his pioneering research offering hope to children with Duchenne muscular dystrophy.

A new 3D model shows that Duchenne gene therapy can repair muscle fibers but fails to shut down the signals that drive scarring.

Punjab and Haryana High Court allowed a disabled wife’s transfer plea after noting her higher degree of disability, child ...

The FDA has put a partial clinical hold on PepGen’s phase 2 mus | The FDA has put a partial clinical hold on PepGen’s phase 2 muscle wasting trial after reviewing preclinical data, continuing the stop ...

Cure Rare Disease (CRD), a non-profit biotechnology organization, today announced a landmark partnership with the LGMD2L Foundation. This collaboration is backed by a generous commitment of $7.65 ...

LVEF (Left Ventricular Ejection Fraction): Percentage measure of how much blood the left ventricle pumps out with each ...

The 41-year-old, from Hamilton, Glasgow, will join Muscular Dystrophy UK, the leading charity for more than 110,000 children and adults in the UK living with ...

While some chief executives have left for personal reasons, others have been ousted amid poor company performance.

Good afternoon, and welcome to Cumberland Pharmaceuticals 2025 Financial Report and Company Update. This call is being recorded at the company's request and will be archived on its website for 1 year ...

Keros Therapeutics, Inc. (“Keros” or the “Company”) (Nasdaq: KROS), a clinical-stage biopharmaceutical company focused on developing and commercializing novel therapeutics to treat a wide range of ...

Agency officials promise fast reviews of new treatments while vowing they will not be a “rubber stamp” for the industry. But ...