A new 3D model shows that Duchenne gene therapy can repair muscle fibers but fails to shut down the signals that drive ...

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

UCL’s Professor Francesco Muntoni has received the 2026 Novo Nordisk Prize for his pioneering research offering hope to children with Duchenne muscular dystrophy.

The FDA has put a partial clinical hold on PepGen’s phase 2 mus | The FDA has put a partial clinical hold on PepGen’s phase 2 muscle wasting trial after reviewing preclinical data, continuing the stop ...

Satellos Bioscience Inc. (NASDAQ: MSLE, TSX: MSCL) (“Satellos” or the “Company”), a clinical-stage biotechnology company developing life-improving medicines to treat degenerative muscle diseases, ...

PHOENIX — Jace Taylor is a rambunctious 4-year-old boy. He runs, jumps and plays with his friends. He isn’t aware that genetically, he’s different from other children. “I think he’s too young to ...

Cure Rare Disease (CRD), a non-profit biotechnology organization, today announced a landmark partnership with the LGMD2L Foundation. This collaboration is backed by a generous commitment of $7.65 ...

Punjab and Haryana High Court allowed a disabled wife’s transfer plea after noting her higher degree of disability, child custody, and difficulty commuting to defend the matrimonial case.

LVEF (Left Ventricular Ejection Fraction): Percentage measure of how much blood the left ventricle pumps out with each ...

The 41-year-old, from Hamilton, Glasgow, will join Muscular Dystrophy UK, the leading charity for more than 110,000 children and adults in the UK living with ...

While some chief executives have left for personal reasons, others have been ousted amid poor company performance.

From sleep disruptions to a hormonal overlap that can make MS harder to manage, this week's health news hits close to home ...