Long-term data from DEVOTE/ONWARD studies show benefits of high dose nusinersen in people living with spinal muscular atrophy (SMA)New Phase 1b data further illustrate potential of salanersen in SMA, ...

A RECOMMENDATION for the HSE not to cover the cost of a drug to help children with a rare muscular disease has been blasted by families. Last year, The Irish Sun highlighted the plight of ...

The agency acted after reviewing mouse data submitted in 2024, making the timing of the new pause “confusing,” one analyst wrote.

A new 3D model shows that Duchenne gene therapy can repair muscle fibers but fails to shut down the signals that drive ...

For sura-vec in wet AMD, top line data from pivotal studies ATMOSPHERE and ASCENT are anticipated in Q4. First patient dosing in NAVIGATE for diabetic retinopathy is planned next quarter, expected to ...

Regenxbio Inc (RGNX) showcases robust pipeline progress and financial stability, despite regulatory challenges.

The Staff Selection Commission has revised disability eligibility for several SSC CGL 2025 posts. A new annexure details ...

An executive assistant's rapid rise and unexpected departure fueled a seismic shift in Michigan football, triggering ...

Doctors warn that Bulgaria’s healthcare system still lacks a sustainable framework for genomic diagnostics, patients are paying the price ...

Actress Aahana Kumra shared glimpses from her trip to Florence, calling the experience of witnessing the city’s iconic art and history in person “unforgettable.” Taking to Instagram, the ...

The document lists the names and roll numbers of recommended candidates in order of merit at upsc.gov.in and ...

Agency officials promise fast reviews of new treatments while vowing they will not be a “rubber stamp” for the industry. But ...