Long-term data from DEVOTE/ONWARD studies show benefits of high dose nusinersen in people living with spinal muscular atrophy (SMA)New Phase 1b data further illustrate potential of salanersen in SMA, ...

Biogen has launched a trio of Phase 3 trials to test salanersen, a new SMA treatment that aims to be a more convenient ...

Union Minister H D Kumaraswamy has assured assistance for a two-year-old child suffering from a rare genetic disorder after ...

LEIGH-ANNE Pinnock has broken her silence on her former Little Mix co-star Jesy Nelson’s twins “awful, heartbreaking” SMA ...

The singer, 34, said she had reached out to her former bandmate after she found out her twin daughters may not live beyond the age of two after being diagnosed with genetic neuromuscular disease, ...

In Trumbull County, a local nonprofit will once again be hiding colorful candy-filled eggs in yards this Easter to help a ...

Easter Egg fundraiser to benefit 9-year-old Trumbull County girl with Spinal Muscular Atrophy ...

JESY Nelson has shared an adorable video of her daughter’s “ballerina” leg exercises amid her twins’ SMA diagnosis.

AnnJi Pharmaceutical Co., Ltd. (AnnJi, TWSE: 7754) announced its participation in the 2026 International Patient and ...

Former Little Mix singer, Leigh-Anne Pinnock, has broken her silence on co-star Jesy Nelson and her twins' heartbreaking SMA diagnosis. The star, who is now working on her solo career, opened up in an ...

Journalist Olha Khudetska, who previously exposed abuses in fundraising for the treatment of Nazariy Husakov (a Lviv resident with spinal muscular atrophy), has drawn attention to the activities of ...

VY1706 clinical entry and VY7523 clinical data anticipated H2 2026 - - Validating brain-targeted capsids in humans: expect ...