K-Pop idol Jang Yeojun of the boy band 'Close Your Eyes' has been diagnosed with rhabdomyolysis. Here is what the muscle ...

The only drug-related adverse events observed are typically anticipated with gene therapy administration, the company noted. ・It added that a proactive, short-course immune modulation regimen in ...

A San Antonio family is asking the community for support as their 12-year-old son lives with a rare genetic disease that ...

On World Rare Disease Day, we take a look at Pompe disease - a rare genetic disorder caused by a deficiency of the GAA enzyme, leading to glycogen buildup in muscles. It results in progressive muscle ...

Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal ...

At the 2026 MDA Conference in Orlando, Genethon unveiled new two‑year efficacy data for its gene therapy candidate GNT0004, a key milestone for Duchenne muscular dystrophy research.

Edgewise Therapeutics, Inc. (Nasdaq: EWTX), a leading muscle disease biopharmaceutical company, today presented at the 2026 MDA Clinical and Scientific Conference, long-term data from its MESA ...

A RECOMMENDATION for the HSE not to cover the cost of a drug to help children with a rare muscular disease has been blasted by families. Last year, The Irish Sun highlighted the plight of ...

Interim observations from the Phase 2 TRAILHEAD study show continued improvement in handgrip strength, overall stability of elbow and shoulder strength in new dynamometry measurements Greater ...

Taking collagen supplements regularly supports bone and muscle health in adults, improving strength and quality of life.

March 4 (Reuters) - PepGen said on Wednesday that the U.S. Food and Drug Administration has placed a partial clinical hold on its mid‑stage trial of a rare muscle disease drug, sending its shares ...

Incubated by Atlas Venture, the biotech startup is advancing a daily pill it sees potentially helping people with dystonia or ...