Data presented at the 2026 Muscular Dystrophy Association meeting could have readthroughs to companies developing therapies ...

Add Yahoo as a preferred source to see more of our stories on Google. Biogen said the trial touted the once-yearly dosing potential of the ASO. Credit: Tada Images / Shutterstock.com (Tada Images / ...

SMA mutations disrupt spinal cord development, with fewer nerve cells in early stages. SMN protein deficiency leads to a mesodermal fate bias, with fewer motor neurons. Increasing SOX2 pathway ...

US biotech major Biogen has presented additional results from the Phase Ib study of salanersen, an investigational novel ...

SMA newborn screening may help infants start treatment sooner, which researchers say could support better motor development outcomes.

STELLAR-2, a randomized, double-blind, sham-controlled study, will evaluate the effects of salanersen when initiated ~6 months after onasemnogene abeparvovec-xioi in infants with SMA who received ...

Jesy Nelson's Little Mix bandmate, Leigh-Anne Pinnock, has opened up about Jesy's twins' diagnosis. Earlier this year, Jesy took to Instagram to announce her twin girls, Ocean Jade and Story Monroe ...

Good morning, everyone. My name is Etzer Darout, senior biotech analyst at Barclays. It's my pleasure to have Scholar Rock with us this morning. With us on stage, we have David Hallal, Chief Executive ...

More early-stage data show the drug, called salanersen, appeared to have positive effects on neurodegeneration and motor function in patients previously treated with Novartis' Zolgensma.

When winter sets in and food becomes scarce, some mammals hibernate, entering a state of deep rest that slashes their energy needs and allows them to fast for months. However, fasting deprives them of ...

It isn't hard to see what makes Maine Coons such widely beloved cats all over the world. With their rugged builds, ...

Permanent; Fitzroy location; Challenging and rewarding work environment; About the Role An opportunity is available for a Grade 3 Physiotherapist to join the ...