Genethon, a pioneer and leader in gene therapy for rare diseases, unveiled results at the MDA Conference in Orlando confirming the long-term efficacy of its GNT0004 gene therapy in Duchenne muscular ...

For a heart just damaged by a blocked artery, timing matters. So does access. That is what makes a new experimental treatment ...

Add Yahoo as a preferred source to see more of our stories on Google. A single self‑amplifying RNA injection that boosts a heart‑healing peptide cut scarring and improved function after heart attacks ...

FDA now permits Arexvy for adults 18–49 with elevated RSV risk from conditions such as chronic cardiopulmonary or renal disease, obesity, and diabetes. Epidemiology in U.S. adults 18–49 includes ...

Four patients with LGMD-R5 (gamma-sarcoglycanopathy, formerly LGMD-2C) have received the ATA-200 gene therapy as part of the ongoing Phase 1b/2 trial evaluating the safety, pharmacodynamics, and ...

The company's clinical development plan comprises three global Phase III studies, including two focused on infants and a third for older patients.

Our cosmetic enhancements have made it to other species, with treatments such as Botox, steroids for muscle tone, and even ...

Brianna "Chickenfry" LaPaglia, in a March 10 TikTok video, got candid about the growing use of GLP-1 weight loss medication.

Spinraza treatment led to sustained improvements in motor function in adults with SMA, according to a South Korean study.

Proper pullet vaccination underpins the protection of layers and broiler breeders during the rearing phase. When done correctly, it stabilises egg ...

Biogen has launched a trio of Phase 3 trials to test salanersen, a new SMA treatment that aims to be a more convenient ...

Even supermodels need a little on-set skincare boost.