The MDA meeting is a key opportunity to highlight the expanding real‑world evidence shaping care for the Duchenne community,” said Will Andrews, MD, Chief Medical Officer of Catalyst. “Through our ...

Solid Biosciences Inc. (Nasdaq: SLDB), a life sciences company developing precision genetic medicines for neuromuscular and cardiac diseases, today announced presentations on SGT-003, its ...

A RECOMMENDATION for the HSE not to cover the cost of a drug to help children with a rare muscular disease has been blasted ...

The agency acted after reviewing mouse data submitted in 2024, making the timing of the new pause “confusing,” one analyst ...

Duchenne muscular dystrophy (DMD) is the most common X-linked neuromuscular disease. It is caused by mutations in the DMD gene that lead to abnormalities of dystrophin protein expression in muscle.

Muscular dystrophy (MD) is a progressive genetic illness that causes muscle strength and function to deteriorate over time. With more than 30 types of MD, symptoms and progression rates vary ...

REGENXBIO Inc. (Nasdaq: RGNX) today announced presentations on its RGX-202 investigational gene therapy for Duchenne muscular dystrophy at the 2026 Muscular Dystrophy Association (MDA) Clinical & ...

Seven-year-old William, a Southern Oregon boy living with Duchenne muscular dystrophy, is going to get a never-before-tried ...

Inactivity, such as bed rest and even sitting for long periods of time, can worsen muscular dystrophy (MD). Remaining physically active can keep you in the best condition to do everyday life ...

New sequencing technologies, including whole-exome and whole-genome sequencing, combined with increased data sharing and international research collaborations, are resulting in the identification of ...

As Jerry Lewis' annual telethon raises a record $65 million for children with the muscle-wasting disease, we find out more from a geneticist Comedian Jerry Lewis says he was surprised to reel in $1.2 ...

Data are scarce regarding the benefits of strength training for muscular dystrophies, for which there are no cures. Strength training to ameliorate the effects of muscular dystrophies (MDs) was found ...