The US Food and Drug Administration (FDA) has created a new pathway to bring personalised therapies to market that can bypass certain requirements, using the success of Baby KJ’s treatment as a ...

Sarah Diepstraten receives funding from the National Health and Medical Research Council, Cure Cancer Australia and My Room Children's Cancer Charity. John (Eddie) La Marca receives funding from ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are glimpses of forward momentum as Vertex and Genetix Bio provide updates.

Researchers discover that hearing-essential proteins (TMC1/TMC2) also regulate cell membranes, and their malfunction is a primary cause of permanent hearing loss.

Proteins long known to be essential for hearing have been hiding a talent: they also act as gatekeepers that shuffle fatty molecules across cell membranes. When this newly discovered function goes ...

Jayashri Kulkarni receives funding from the National Health and Medical Research Council as a Leadership Level 3 Investigator Grant, and has received clinical trials funding from pharmaceutical ...

Athletic director Gene Taylor fired Jerome Tang 'for cause' over remarks about players. Tang compiled 71-57 record after Elite Eight debut; K‑State faces 3rd straight NCAA miss. Taylor named Matthew ...

A new study published in the Journal of Psychopathology and Clinical Science offers a nuanced look at how genetic risk for depression interacts with social and economic life circumstances to influence ...

Florida state Rep. Adam Anderson championed the Sunshine Genetics Act, the first state-backed genetic disease screening program in the nation. Anderson's son, Drew, died in 2019 from Tay-Sachs disease ...

Psychiatric disorders can share common genetic influences, which means parts of DNA can be at the root of more than one mental condition, new research has found. The study, led by researchers at Texas ...

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited blindness. Their study shows that changes in specific pieces of DNA, which ...