The diagnosis and management of CIDP are complex and best addressed by an interprofessional health care team that includes neurologists, neuromuscular specialists, physical medicine and rehabilitation ...

Test Your Knowledge About the Signs and Symptoms of HDFN Test Your Knowledge About the Guidelines for HDFN Test Your Knowledge About Therapies for HDFN Test Your ...

Get the latest news, resources, and perspectives on idiopathic pulmonary fibrosis (IPF), written specifically for HCPs who treat the disease.

Overall, the life expectancy of patients with SCD is lower than that of persons without SCD. 1 However, life expectancy varies depending on the type of disease, treatments administered, and ...

Chronic inflammatory demyelinating polyneuropathy (CIDP) is a rare acquired autoimmune neurological disorder in which both T-cell-mediated and humoral immune mechanisms target healthy myelinated ...

Test Your Knowledge About Eteplirsen for the Treatment of DMD Test Your Knowledge About the Treatment of DMD Test Your Knowledge About the Epidemiology of DMD Test ...

Get the latest news, resources, and perspectives on spinal muscular atrophy (SMA), written specifically for HCPs who treat the disease.

Researchers recently detailed the genetic and clinical features of congenital protein-losing enteropathy (PLE), with a focus on CHAPLE disease.

Test Your Knowledge About the Signs and Symptoms of FNAIT Test Your Knowledge About the Epidemiology of FNAIT Test Your Knowledge About the Diagnosis of FNAIT Rare Disease Advisor, a trusted source of ...

Fetal and neonatal alloimmune thrombocytopenia (FNAIT) is a rare immune‐mediated hematological disorder caused by alloantibodies to human platelet antigens (HPA). It can cause severe thrombocytopenia ...

SMA is a rare disease with an estimated incidence of 1 in 10,000 live births. The prevalence is estimated to be approximately 1 to 2 per 100,000 persons and is influenced by the drastically shortened ...

The recommendations were based on the available evidence, its certainty, and key judgments using the Grading of Recommendations Assessment, Development and Evaluation framework. New guidelines ...